Re: Gene therapy trials treat inherited blindness and deafness

On Mon, 13 May 2024 11:54:22 +0200, D <nospam@example.net> wrote:

gene therapy treatment

What is gene therapy used to treat?

Gene therapy aims to fix a faulty gene or replace it with a healthy
gene to try to cure disease or make the body better able to fight
disease. It holds promise as a treatment for a wide range of diseases,
such as cancer, cystic fibrosis, heart disease, diabetes, hemophilia
and AIDS.

The U.S. Food and Drug Administration (FDA) has approved gene therapy
products for several conditions, including cancer, spinal muscular
atrophy, hemophilia and sickle cell disease. But for most people, gene
therapy is available only as part of a clinical trial.


https://www.mayoclinic.org/tests-procedures/gene-therapy/about/pac-20384619